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Category: Gene Therapy

Validation of qPCR Assays for Gene Therapy

Though the modern world has progressed a lot in terms of medical interventions and biomedicine, there still are a vast number of diseases and disorders…

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The Power of Being NYCE

A recent study using triple-edited ‘NYCE’ cells shows the possibilities of multiplex genome editing to effectively treat complex diseases like some cancers. We explore the…

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Your Questions About Immunogenicity Assessment of Gene Therapy Compounds Answered

The webinar I recently hosted with my colleague Lydia Michaut explored key challenges and trends in the immunogenicity assessment of gene therapy compounds. This recap…

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Immunogenicity Assessment of Gene Therapy Compounds

By Dr. Arno Kromminga and Dr. Lydia Michaut

Gene therapy has experienced an exciting resurgence in the post-genomic era, but unwanted immunogenicity is still a…

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The FDA’s Response to an Increase in the Development of Gene and Cell Therapies: What It Means for Sponsors

...material, gene therapy uses DNA to manipulate a patient’s cells to compensate for abnormal genes or to make a beneficial protein, and cell therapy

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